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Antisense Oligo-Mediated Multiple Exon Skipping in a Dog Model of Duchenne Muscular Dystrophy

Exon skipping is currently one of the most promising molecular therapies for Duchenne muscular dystrophy (DMD). We have recently developed multiple exon skipping targeting exons 6 and 8 in dystrophin mRNA of canine X-linked muscular dystrophy (CXMD), an animal model of DMD, which exhibits severe dys...

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Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:Methods Mol Biol
Egile Nagusiak: Yokota, Toshifumi, Hoffman, Eric, Takeda, Shin’ichi
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: 2011
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC4491489/
https://ncbi.nlm.nih.gov/pubmed/21194037
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/978-1-61737-982-6_20
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