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New, Tolerable γ-Secretase Inhibitor Takes Desmoid Down a Notch

A phase I trial of PF-03084014, an oral reversible γ-secretase inhibitor (GSI), in solid tumor malignancies shows drug tolerability in patients. Evidence of Notch pathway inhibition was demonstrated in peripheral blood. A surprisingly high rate of response was seen in desmoid tumors, a rare but ofte...

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Publicat a:Clin Cancer Res
Autors principals: Hughes, Dennis P.M., Kummar, Shivaani, Lazar, Alexander J.
Format: Artigo
Idioma:Inglês
Publicat: 2014
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4306586/
https://ncbi.nlm.nih.gov/pubmed/25336699
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1158/1078-0432.CCR-14-1660
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