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Criteria for evaluating response and outcome in clinical trials for children with juvenile myelomonocytic leukemia

Juvenile myelomonocytic leukemia is a rare myeloproliferative disease in young children. While hematopoietic stem cell transplantation remains the only curative therapeutic option for most patients, children with juvenile myelomonocytic leukemia increasingly receive novel agents in phase I–II clinic...

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Publicat a:Haematologica
Autors principals: Niemeyer, Charlotte M., Loh, Mignon L., Cseh, Annamaria, Cooper, Todd, Dvorak, Christopher C., Chan, Rebecca, Xicoy, Blanca, Germing, Ulrich, Kojima, Seiji, Manabe, Atsushi, Dworzak, Michael, De Moerloose, Barbara, Starý, Jan, Smith, Owen P., Masetti, Riccardo, Catala, Albert, Bergstraesser, Eva, Ussowicz, Marek, Fabri, Oskana, Baruchel, André, Cavé, Hélène, Zwaan, Michel, Locatelli, Franco, Hasle, Henrik, van den Heuvel-Eibrink, Marry M., Flotho, Christian, Yoshimi, Ayami
Format: Artigo
Idioma:Inglês
Publicat: Ferrata Storti Foundation 2015
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4281308/
https://ncbi.nlm.nih.gov/pubmed/25552679
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3324/haematol.2014.109892
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