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Criteria for evaluating response and outcome in clinical trials for children with juvenile myelomonocytic leukemia

Juvenile myelomonocytic leukemia is a rare myeloproliferative disease in young children. While hematopoietic stem cell transplantation remains the only curative therapeutic option for most patients, children with juvenile myelomonocytic leukemia increasingly receive novel agents in phase I–II clinic...

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Detalhes bibliográficos
Publicado no:Haematologica
Main Authors: Niemeyer, Charlotte M., Loh, Mignon L., Cseh, Annamaria, Cooper, Todd, Dvorak, Christopher C., Chan, Rebecca, Xicoy, Blanca, Germing, Ulrich, Kojima, Seiji, Manabe, Atsushi, Dworzak, Michael, De Moerloose, Barbara, Starý, Jan, Smith, Owen P., Masetti, Riccardo, Catala, Albert, Bergstraesser, Eva, Ussowicz, Marek, Fabri, Oskana, Baruchel, André, Cavé, Hélène, Zwaan, Michel, Locatelli, Franco, Hasle, Henrik, van den Heuvel-Eibrink, Marry M., Flotho, Christian, Yoshimi, Ayami
Formato: Artigo
Idioma:Inglês
Publicado em: Ferrata Storti Foundation 2015
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC4281308/
https://ncbi.nlm.nih.gov/pubmed/25552679
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3324/haematol.2014.109892
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