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A Renaissance for Antisense Oligonucleotide Drugs in Neurology: Exon Skipping Breaks New Ground

Antisense oligonucleotides are short nucleic acid sequences designed for use as small-molecule drugs. They recognize and bind to specific messenger RNA (mRNA) or pre-mRNA sequences to create small double-stranded regions of the target mRNA that alter mRNA splicing patterns or inhibit protein transla...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Egile Nagusiak: Yokota, Toshifumi, Takeda, Shin'ichi, Lu, Qi-Long, Partridge, Terence A., Nakamura, Akinori, Hoffman, Eric P.
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: 2009
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC4111150/
https://ncbi.nlm.nih.gov/pubmed/19139297
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1001/archneurol.2008.540
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