Laddar...

In Vitro Multiexon Skipping by Antisense PMOs in Dystrophic Dog and Exon 7-Deleted DMD Patient

Antisense oligonucleotide induced exon skipping emerges as a promising therapeutic strategy for patients suffering from a devastating muscle disorder Duchenne muscular dystrophy (DMD). Systemic administration of antisense phosphorodiamidate morpholino oligomers (PMOs) targeting exons 6 and 8 in dyst...

Full beskrivning

Sparad:
Bibliografiska uppgifter
I publikationen:Methods Mol Biol
Huvudupphovsmän: Nakamura, Akinori, Aoki, Yoshitsugu, Tsoumpra, Maria, Yokota, Toshifumi, Takeda, Shin’ichi
Materialtyp: Artigo
Språk:Inglês
Publicerad: 2018
Ämnen:
Länkar:https://ncbi.nlm.nih.gov/pmc/articles/PMC6557157/
https://ncbi.nlm.nih.gov/pubmed/30171540
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/978-1-4939-8651-4_9
Taggar: Lägg till en tagg
Inga taggar, Lägg till första taggen!