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Severe neuromuscular denervation of clinically relevant muscles in a mouse model of spinal muscular atrophy

Spinal muscular atrophy (SMA), a motoneuron disease caused by a deficiency of the survival of motor neuron (SMN) protein, is characterized by motoneuron loss and muscle weakness. It remains unclear whether widespread loss of neuromuscular junctions (NMJs) is involved in SMA pathogenesis. We undertoo...

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Autors principals: Ling, Karen K. Y., Gibbs, Rebecca M., Feng, Zhihua, Ko, Chien-Ping
Format: Artigo
Idioma:Inglês
Publicat: Oxford University Press 2012
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Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC3235013/
https://ncbi.nlm.nih.gov/pubmed/21968514
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/hmg/ddr453
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