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Incorporation of Pseudouridine Into mRNA Yields Superior Nonimmunogenic Vector With Increased Translational Capacity and Biological Stability

In vitro–transcribed mRNAs encoding physiologically important proteins have considerable potential for therapeutic applications. However, in its present form, mRNA is unfeasible for clinical use because of its labile and immunogenic nature. Here, we investigated whether incorporation of naturally mo...

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Autors principals: Karikó, Katalin, Muramatsu, Hiromi, Welsh, Frank A, Ludwig, János, Kato, Hiroki, Akira, Shizuo, Weissman, Drew
Format: Artigo
Idioma:Inglês
Publicat: 2008
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Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC2775451/
https://ncbi.nlm.nih.gov/pubmed/18797453
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/mt.2008.200
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