Загрузка...

Novel Adeno-Associated Virus Serotypes Efficiently Transduce Murine Photoreceptors

Severe inherited retinal diseases, such as retinitis pigmentosa and Leber congenital amaurosis, are caused by mutations in genes preferentially expressed in photoreceptors. While adeno-associated virus (AAV)-mediated gene transfer can correct retinal pigment epithelium (RPE) defects in animal models...

Полное описание

Сохранить в:
Библиографические подробности
Главные авторы: Allocca, Mariacarmela, Mussolino, Claudio, Garcia-Hoyos, Maria, Sanges, Daniela, Iodice, Carolina, Petrillo, Marco, Vandenberghe, Luk H., Wilson, James M., Marigo, Valeria, Surace, Enrico M., Auricchio, Alberto
Формат: Artigo
Язык:Inglês
Опубликовано: American Society for Microbiology 2007
Предметы:
Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC2045569/
https://ncbi.nlm.nih.gov/pubmed/17699581
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1128/JVI.01327-07
Метки: Добавить метку
Нет меток, Требуется 1-ая метка записи!