What Is Next for Retinal Gene Therapy?

по Vandenberghe, Luk H.
Опубликовано в: Cold Spring Harb Perspect Med (2015)

AAV Engineering Identifies a Species Barrier That Highlights a Portal to the Brain

по Vandenberghe, Luk H.
Опубликовано в: Mol Ther (2019)

Adeno-associated Virus: Fit to serve

по Zinn, Eric, Vandenberghe, Luk H.
Опубликовано 2014

Promising and delivering gene therapies for vision loss

по Carvalho, Livia S., Vandenberghe, Luk H.
Опубликовано в: Vision Res (2014)

Gene Therapy for Deaf Mice Goes Viral

по Holt, Jeffrey R, Vandenberghe, Luk H
Опубликовано 2012

Retinal Gene Therapy Coming of Age

по Cepko, Connie L., Vandenberghe, Luk H.
Опубликовано в: Hum Gene Ther (2013)

Breaking and Sealing Barriers in Retinal Gene Therapy

по Miller, Joan W., Vandenberghe, Luk H.
Опубликовано в: Mol Ther (2018)

Quantitative and Digital Droplet-Based AAV Genome Titration

по Sanmiguel, Julio, Gao, Guangping, Vandenberghe, Luk H.
Опубликовано в: Methods Mol Biol (2019)

Hepatic regulatory T cells and Kupffer cells are crucial mediators of systemic T cell tolerance to antigens targeting murine liver

по Breous, Ekaterina, Somanathan, Suryanarayan, Vandenberghe, Luk H., Wilson, James M.
Опубликовано в: Hepatology (2009)

Single stranded adeno-associated virus achieves efficient gene transfer to anterior segment in the mouse eye

по Wang, Li, Xiao, Ru, Andres-Mateos, Eva, Vandenberghe, Luk H.
Опубликовано в: PLoS One (2017)

Residues on Adeno-associated Virus Capsid Lumen Dictate Interactions and Compatibility with the Assembly-Activating Protein

по Maurer, Anna C., Cepeda Diaz, Ana Karla, Vandenberghe, Luk H.
Опубликовано в: J Virol (2019)

Controlling AAV Tropism in the Nervous System with Natural and Engineered Capsids

по Castle, Michael J., Turunen, Heikki T., Vandenberghe, Luk H., Wolfe, John H.
Опубликовано в: Methods Mol Biol (2016)

Cochlear gene therapy with ancestral AAV in adult mice: complete transduction of inner hair cells without cochlear dysfunction

по Suzuki, Jun, Hashimoto, Ken, Xiao, Ru, Vandenberghe, Luk H., Liberman, M. Charles
Опубликовано в: Sci Rep (2017)

Corrigendum: Cochlear gene therapy with ancestral AAV in adult mice: complete transduction of inner hair cells without cochlear dysfunction

по Suzuki, Jun, Hashimoto, Ken, Xiao, Ru, Vandenberghe, Luk H., Liberman, M. Charles
Опубликовано в: Sci Rep (2017)

Efficient Gene Transfer to Kidney Mesenchymal Cells Using a Synthetic Adeno-Associated Viral Vector

по Ikeda, Yoichiro, Sun, Zhao, Ru, Xiao, Vandenberghe, Luk H., Humphreys, Benjamin D.
Опубликовано в: J Am Soc Nephrol (2018)

Impact of Preexisting Vector Immunity on the Efficacy of Adeno-Associated Virus-Based HIV-1 Gag Vaccines

по Lin, Jianping, Calcedo, Roberto, Vandenberghe, Luk H., Figueredo, Joanita M., Wilson, James M.
Опубликовано 2008

Exosome-associated AAV2 vector mediates robust gene delivery into the murine retina upon intravitreal injection

по Wassmer, Sarah J., Carvalho, Livia S., György, Bence, Vandenberghe, Luk H., Maguire, Casey A.
Опубликовано в: Sci Rep (2017)

Host Immune Responses to Chronic Adenovirus Infections in Human and Nonhuman Primates

по Calcedo, Roberto, Vandenberghe, Luk H., Roy, Soumitra, Somanathan, Suryanarayan, Wang, Lili, Wilson, James M.
Опубликовано 2009

A New Genetic Vaccine Platform Based on an Adeno-Associated Virus Isolated from a Rhesus Macaque

по Lin, Jianping, Calcedo, Roberto, Vandenberghe, Luk H., Bell, Peter, Somanathan, Suryanarayan, Wilson, James M.
Опубликовано 2009

Transduction Efficiencies of Novel AAV Vectors in Mouse Airway Epithelium In Vivo and Human Ciliated Airway Epithelium In Vitro

по Limberis, Maria P, Vandenberghe, Luk H, Zhang, Liqun, Pickles, Raymond J, Wilson, James M
Опубликовано 2008