Targeting SR Proteins Improves SMN Expression in Spinal Muscular Atrophy Cells

Por Wee, Claribel D., Havens, Mallory A., Jodelka, Francine M., Hastings, Michelle L.
Publicado no PLoS One (2014)

Inhibition of myostatin does not ameliorate disease features of severe spinal muscular atrophy mice

Por Sumner, Charlotte J., Wee, Claribel D., Warsing, Leigh C., Choe, Dong W., Ng, Andrew S., Lutz, Cathleen, Wagner, Kathryn R.
Publicado em 2009

Increased IGF-1 in muscle modulates the phenotype of severe SMA mice

Por Bosch-Marcé, Marta, Wee, Claribel D., Martinez, Tara L., Lipkes, Celeste E., Choe, Dong W., Kong, Lingling, Van Meerbeke, James P., Musarò, Antonio, Sumner, Charlotte J.
Publicado em 2011

The DcpS inhibitor RG3039 improves motor function in SMA mice

Por Van Meerbeke, James P., Gibbs, Rebecca M., Plasterer, Heather L., Miao, Wenyan, Feng, Zhihua, Lin, Ming-Yi, Rucki, Agnieszka A., Wee, Claribel D., Xia, Bing, Sharma, Shefali, Jacques, Vincent, Li, Darrick K., Pellizzoni, Livio, Rusche, James R., Ko, Chien-Ping, Sumner, Charlotte J.
Publicado em 2013