Immune response hinders therapy for lysosomal storage diseases

по Ponder, Katherine P.
Опубликовано 2008

Hemophilia Gene Therapy: A Holy Grail Found

по Ponder, Katherine P
Опубликовано 2011

Their Just Rewards: Acknowledging Key Contributions of Society Members

по Ponder, Katherine P
Опубликовано 2013

Gene therapy for mucopolysaccharidosis

по Ponder, Katherine P, Haskins, Mark E
Опубликовано 2007

The effect of Tlr4 and/or C3 Deficiency and of Neonatal Gene Therapy on Skeletal Disease in Mucopolysaccharidosis VII mice

по Xing, Elizabeth M., Wu, Susan, Ponder, Katherine P.
Опубликовано в: Mol Genet Metab (2014)

Neonatal Intravenous Injection of a Gammaretroviral Vector Has a Low Incidence of Tumor Induction in Mice

по Tittiger, Mindy, Ma, Xiucui, Xu, Lingfei, Ponder, Katherine P.
Опубликовано 2008

Gene therapy for cardiovascular manifestations of lysosomal storage diseases

по Sleeper, Meg M., Haskins, Mark E., Ponder, Katherine P.
Опубликовано в: Heart Metab (2008)

Mechanism of Shortened Bones in Mucopolysaccharidosis VII

по Metcalf, Jason A., Zhang, Yanming, Hilton, Matthew J., Long, Fanxin, Ponder, Katherine P.
Опубликовано 2009

Improved Retroviral Vector Design Results in Sustained Expression after Adult Gene Therapy in Mucopolysaccharidosis I Mice

по Herati, Ramin Sedaghat, Ma, Xiucui, Tittiger, Mindy, Ohlemiller, Kevin K, Kovacs, Attila, Ponder, Katherine P.
Опубликовано 2008

Retroviral Vector-mediated Gene Therapy to Mucopolysaccharidosis I Mice Improves Sensorimotor Impairments and Other Behavior Deficits

по Baldo, Guilherme, Wozniak, David F., Ohlemiller, Kevin K., Zhang, Yanming, Giugliani, Roberto, Ponder, Katherine P.
Опубликовано 2012

Absence of a desmopressin response after therapeutic expression of factor VIII in hemophilia A dogs with liver-directed neonatal gene therapy

по Xu, Lingfei, Nichols, Timothy C., Sarkar, Rita, McCorquodale, Stephanie, Bellinger, Dwight A., Ponder, Katherine P.
Опубликовано 2005

Altered lumbar spine structure, biochemistry and biomechanical properties in a canine model of mucopolysaccharidosis type VII

по Smith, Lachlan J, Martin, John T, Szczesny, Spencer E, Ponder, Katherine P, Haskins, Mark E, Elliott, Dawn M
Опубликовано 2010

Upregulation of elastase proteins results in aortic dilatation in mucopolysaccharidosis I mice

по Ma, Xiucui, Tittiger, Mindy, Knutsen, Russell H., Kovacs, Attila, Schaller, Laura, Mecham, Robert P., Ponder, Katherine P.
Опубликовано 2008

Radiographic Evaluation of Bones and Joints in Mucopolysaccharidosis I and VII Dogs After Neonatal Gene Therapy

по Herati, Ramin Sedaghat, Knox, Van W., O’Donnell, Patricia, D’Angelo, Marina, Haskins, Mark E., Ponder, Katherine P.
Опубликовано 2008

Evidence of a progressive motor dysfunction in Mucopolysaccharidosis type I mice

по Baldo, Guilherme, Mayer, Fabiana Quoos, Martinelli, Barbara, Dilda, Anna, Meyer, Fabiola, Ponder, Katherine P., Giugliani, Roberto, Matte, Ursula
Опубликовано 2012

A Review of Gene Therapy in Canine and Feline Models of Lysosomal Storage Disorders

по Bradbury, Allison M., Gurda, Brittney L., Casal, Margret L., Ponder, Katherine P., Vite, Charles H., Haskins, Mark E.
Опубликовано в: Hum Gene Ther Clin Dev (2015)

Clinical characterization of cardiovascular abnormalities associated with feline mucopolysaccharidosis I and VI

по Sleeper, Meg M., Kusiak, Catherine M., Shofer, Frances S., O’Donnell, Patricia, Bryan, Caroline, Ponder, Katherine P., Haskins, Mark E.
Опубликовано 2008

Effect of neonatal gene therapy on lumbar spine disease in mucopolysaccharidosis VII dogs

по Smith, Lachlan J, Martin, John T, O'Donnell, Patricia, Wang, Ping, Elliott, Dawn M, Haskins, Mark E, Ponder, Katherine P
Опубликовано 2012

Effects of Neonatal Enzyme Replacement Therapy and Simvastatin Treatment on Cervical Spine Disease in Mucopolysaccharidosis I Dogs

по Chiaro, Joseph A, O’Donnell, Patricia, Shore, Eileen M, Malhotra, Neil R, Ponder, Katherine P, Haskins, Mark E, Smith, Lachlan J
Опубликовано в: J Bone Miner Res (2014)

Upregulation of Elastase Activity in Aorta in Mucopolysaccharidosis I and VII Dogs May be Due to Increased Cytokine Expression

по Metcalf, Jason A., Linders, Bruce, Wu, Susan, Bigg, Paul, O’Donnell, Patricia, Sleeper, Meg M., Whyte, Michael P., Haskins, Mark, Ponder, Katherine P.
Опубликовано 2009