A Review of Gene Therapy in Canine and Feline Models of Lysosomal Storage Disorders

Lysosomal storage disorders (LSDs) are inherited diseases that result from the intracellular accumulation of incompletely degraded macromolecules. The majority of LSDs affect both the peripheral and central nervous systems and are not effectively treated by enzyme replacement therapy, substrate redu...

Fuld beskrivelse

Na minha lista:
Bibliografiske detaljer
Udgivet i:Hum Gene Ther Clin Dev
Main Authors: Bradbury, Allison M., Gurda, Brittney L., Casal, Margret L., Ponder, Katherine P., Vite, Charles H., Haskins, Mark E.
Format: Artigo
Sprog:Inglês
Udgivet: Mary Ann Liebert, Inc. 2015
Fag:
Invited Reviews
Online adgang:https://ncbi.nlm.nih.gov/pmc/articles/PMC4516914/
https://ncbi.nlm.nih.gov/pubmed/25671613
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/humc.2015.002
Tags: Tilføj Tag
Ingen Tags, Vær først til at tagge denne postø!

Lignende værker