Immune response hinders therapy for lysosomal storage diseases

Autor Ponder, Katherine P.
Vydáno 2008

Hemophilia Gene Therapy: A Holy Grail Found

Autor Ponder, Katherine P
Vydáno 2011

Their Just Rewards: Acknowledging Key Contributions of Society Members

Autor Ponder, Katherine P
Vydáno 2013

Gene therapy for mucopolysaccharidosis

Autor Ponder, Katherine P, Haskins, Mark E
Vydáno 2007

The effect of Tlr4 and/or C3 Deficiency and of Neonatal Gene Therapy on Skeletal Disease in Mucopolysaccharidosis VII mice

Autor Xing, Elizabeth M., Wu, Susan, Ponder, Katherine P.
Vydáno v Mol Genet Metab (2014)

Neonatal Intravenous Injection of a Gammaretroviral Vector Has a Low Incidence of Tumor Induction in Mice

Autor Tittiger, Mindy, Ma, Xiucui, Xu, Lingfei, Ponder, Katherine P.
Vydáno 2008

Gene therapy for cardiovascular manifestations of lysosomal storage diseases

Autor Sleeper, Meg M., Haskins, Mark E., Ponder, Katherine P.
Vydáno v Heart Metab (2008)

Mechanism of Shortened Bones in Mucopolysaccharidosis VII

Autor Metcalf, Jason A., Zhang, Yanming, Hilton, Matthew J., Long, Fanxin, Ponder, Katherine P.
Vydáno 2009

Improved Retroviral Vector Design Results in Sustained Expression after Adult Gene Therapy in Mucopolysaccharidosis I Mice

Autor Herati, Ramin Sedaghat, Ma, Xiucui, Tittiger, Mindy, Ohlemiller, Kevin K, Kovacs, Attila, Ponder, Katherine P.
Vydáno 2008

Retroviral Vector-mediated Gene Therapy to Mucopolysaccharidosis I Mice Improves Sensorimotor Impairments and Other Behavior Deficits

Autor Baldo, Guilherme, Wozniak, David F., Ohlemiller, Kevin K., Zhang, Yanming, Giugliani, Roberto, Ponder, Katherine P.
Vydáno 2012

Absence of a desmopressin response after therapeutic expression of factor VIII in hemophilia A dogs with liver-directed neonatal gene therapy

Autor Xu, Lingfei, Nichols, Timothy C., Sarkar, Rita, McCorquodale, Stephanie, Bellinger, Dwight A., Ponder, Katherine P.
Vydáno 2005

Altered lumbar spine structure, biochemistry and biomechanical properties in a canine model of mucopolysaccharidosis type VII

Autor Smith, Lachlan J, Martin, John T, Szczesny, Spencer E, Ponder, Katherine P, Haskins, Mark E, Elliott, Dawn M
Vydáno 2010

Upregulation of elastase proteins results in aortic dilatation in mucopolysaccharidosis I mice

Autor Ma, Xiucui, Tittiger, Mindy, Knutsen, Russell H., Kovacs, Attila, Schaller, Laura, Mecham, Robert P., Ponder, Katherine P.
Vydáno 2008

Radiographic Evaluation of Bones and Joints in Mucopolysaccharidosis I and VII Dogs After Neonatal Gene Therapy

Autor Herati, Ramin Sedaghat, Knox, Van W., O’Donnell, Patricia, D’Angelo, Marina, Haskins, Mark E., Ponder, Katherine P.
Vydáno 2008

Evidence of a progressive motor dysfunction in Mucopolysaccharidosis type I mice

Autor Baldo, Guilherme, Mayer, Fabiana Quoos, Martinelli, Barbara, Dilda, Anna, Meyer, Fabiola, Ponder, Katherine P., Giugliani, Roberto, Matte, Ursula
Vydáno 2012

A Review of Gene Therapy in Canine and Feline Models of Lysosomal Storage Disorders

Autor Bradbury, Allison M., Gurda, Brittney L., Casal, Margret L., Ponder, Katherine P., Vite, Charles H., Haskins, Mark E.
Vydáno v Hum Gene Ther Clin Dev (2015)

Clinical characterization of cardiovascular abnormalities associated with feline mucopolysaccharidosis I and VI

Autor Sleeper, Meg M., Kusiak, Catherine M., Shofer, Frances S., O’Donnell, Patricia, Bryan, Caroline, Ponder, Katherine P., Haskins, Mark E.
Vydáno 2008

Effect of neonatal gene therapy on lumbar spine disease in mucopolysaccharidosis VII dogs

Autor Smith, Lachlan J, Martin, John T, O'Donnell, Patricia, Wang, Ping, Elliott, Dawn M, Haskins, Mark E, Ponder, Katherine P
Vydáno 2012

Effects of Neonatal Enzyme Replacement Therapy and Simvastatin Treatment on Cervical Spine Disease in Mucopolysaccharidosis I Dogs

Autor Chiaro, Joseph A, O’Donnell, Patricia, Shore, Eileen M, Malhotra, Neil R, Ponder, Katherine P, Haskins, Mark E, Smith, Lachlan J
Vydáno v J Bone Miner Res (2014)

Upregulation of Elastase Activity in Aorta in Mucopolysaccharidosis I and VII Dogs May be Due to Increased Cytokine Expression

Autor Metcalf, Jason A., Linders, Bruce, Wu, Susan, Bigg, Paul, O’Donnell, Patricia, Sleeper, Meg M., Whyte, Michael P., Haskins, Mark, Ponder, Katherine P.
Vydáno 2009