Combination therapies for lysosomal storage disease: is the whole greater than the sum of its parts?

di Hawkins-Salsbury, Jacqueline A., Reddy, Adarsh S., Sands, Mark S.
Pubblicazione 2011

Pathogenesis and Therapies for Infantile Neuronal Ceroid Lipofuscinosis (infantile CLN1 disease)

di Hawkins-Salsbury, Jacqueline A., Cooper, Jonathan D., Sands, Mark S.
Pubblicato in Biochim Biophys Acta (2013)

Oxidative Stress as a Therapeutic Target in Globoid Cell Leukodystrophy

di Hawkins-Salsbury, Jacqueline A, Qin, Elizabeth Y, Reddy, Adarsh S, Vogler, Carole A, Sands, Mark S
Pubblicazione 2012

Bone marrow transplantation increases efficacy of central nervous system-directed enzyme replacement therapy in the murine model of globoid cell leukodystrophy

di Qin, Elizabeth Y., Hawkins-Salsbury, Jacqueline A., Jiang, Xuntian, Reddy, Adarsh S., Farber, Nuri B., Ory, Daniel S., Sands, Mark S.
Pubblicazione 2012

Psychosine, the cytotoxic sphingolipid that accumulates in globoid cell leukodystrophy, alters membrane architecture

di Hawkins-Salsbury, Jacqueline A., Parameswar, Archana R., Jiang, Xuntian, Schlesinger, Paul H., Bongarzone, Ernesto, Ory, Daniel S., Demchenko, Alexei V., Sands, Mark S.
Pubblicazione 2013

Mechanism-Based Combination Treatment Dramatically Increases Therapeutic Efficacy in Murine Globoid Cell Leukodystrophy

di Hawkins-Salsbury, Jacqueline A., Shea, Lauren, Jiang, Xuntian, Hunter, Daniel A., Guzman, A. Miguel, Reddy, Adarsh S., Qin, Elizabeth Y., Li, Yedda, Gray, Steven J., Ory, Daniel S., Sands, Mark S.
Pubblicato in J Neurosci (2015)

Bone Marrow Transplantation Augments the Effect of Brain- and Spinal Cord-Directed Adeno-Associated Virus 2/5 Gene Therapy by Altering Inflammation in the Murine Model of Globoid-C...

di Reddy, Adarsh S., Kim, Joong H., Hawkins-Salsbury, Jacqueline A., Macauley, Shannon L., Tracy, Elisabeth T., Vogler, Carole A., Han, Xialin, Song, Sheng-Kwei, Wozniak, David F., Fowler, Stephen C., Klein, Robyn S., Sands, Mark S.
Pubblicazione 2011

Innovations in MD-only physician-scientist training: experiences from the Burroughs Wellcome Fund physician-scientist institutional award initiative

di McElvaine, Allison T., Hawkins-Salsbury, Jacqueline A., Arora, Vineet M., Gladwin, Mark T., Goldenring, James R., Huston, David P., Krakow, Deborah, Rhee, Kyu, Solway, Julian, Steinman, Richard A., Towler, Dwight A., Utz, Paul J., Yokoyama, Wayne M., Simpson, Rolly L., Muglia, Louis J., Permar, Sallie R., Gbadegesin, Rasheed A.
Pubblicato in J Clin Invest (2021)