Long-term Preservation of Cone Photoreceptors and Restoration of Cone Function by Gene Therapy in the Guanylate Cyclase-1 Knockout (GC1KO) Mouse

Autor Boye, Sanford L., Conlon, Thomas, Erger, Kirsten, Ryals, Renee, Neeley, Andy, Cossette, Travis, Pang, Jijing, Dyka, Frank M., Hauswirth, William W., Boye, Shannon E.
Vydáno 2011

Long-term Correction of Very Long-chain Acyl-CoA Dehydrogenase Deficiency in Mice Using AAV9 Gene Therapy

Autor Keeler, Allison M, Conlon, Thomas, Walter, Glenn, Zeng, Huadong, Shaffer, Scott A, Dungtao, Fu, Erger, Kirsten, Cossette, Travis, Tang, Qiushi, Mueller, Christian, Flotte, Terence R
Vydáno 2012

Recombinant AAV Serotype and Capsid Mutant Comparison for Pulmonary Gene Transfer of α-1-Antitrypsin Using Invasive and Noninvasive Delivery

Autor Liqun Wang, Rejean, McLaughlin, Thomas, Cossette, Travis, Tang, Qiushi, Foust, Kevin, Campbell-Thompson, Martha, Martino, Ashley, Cruz, Pedro, Loiler, Scott, Mueller, Christian, Flotte, Terence R
Vydáno 2008

Preclinical Toxicology and Biodistribution Studies of Recombinant Adeno-Associated Virus 1 Human Acid α-Glucosidase

Autor Conlon, Thomas J., Erger, Kirsten, Porvasnik, Stacy, Cossette, Travis, Roberts, Cheryl, Combee, Lynn, Islam, Saleem, Kelley, Jeffry, Cloutier, Denise, Clément, Nathalie, Abernathy, Corinne R., Byrne, Barry J.
Vydáno 2013

Stability and Safety of an AAV Vector for Treating RPGR-ORF15 X-Linked Retinitis Pigmentosa

Autor Deng, Wen-Tao, Dyka, Frank M., Dinculescu, Astra, Li, Jie, Zhu, Ping, Chiodo, Vince A., Boye, Sanford L., Conlon, Thomas J., Erger, Kirsten, Cossette, Travis, Hauswirth, William W.
Vydáno v Hum Gene Ther (2015)

Glycogen Storage Disease Type Ia in Canines: A Model for Human Metabolic and Genetic Liver Disease

Autor Specht, Andrew, Fiske, Laurie, Erger, Kirsten, Cossette, Travis, Verstegen, John, Campbell-Thompson, Martha, Struck, Maggie B., Lee, Young Mok, Chou, Janice Y., Byrne, Barry J., Correia, Catherine E., Mah, Cathryn S., Weinstein, David A., Conlon, Thomas J.
Vydáno 2011

Enhancing face validity of mouse models of Alzheimer’s disease with natural genetic variation

Autor Onos, Kristen D., Uyar, Asli, Keezer, Kelly J., Jackson, Harriet M., Preuss, Christoph, Acklin, Casey J., O’Rourke, Rita, Buchanan, Rebecca, Cossette, Travis L., Sukoff Rizzo, Stacey J., Soto, Ileana, Carter, Gregory W., Howell, Gareth R.
Vydáno v PLoS Genet (2019)

Preclinical Potency and Safety Studies of an AAV2-Mediated Gene Therapy Vector for the Treatment of MERTK Associated Retinitis Pigmentosa

Autor Conlon, Thomas J., Deng, Wen-Tao, Erger, Kirsten, Cossette, Travis, Pang, Ji-jing, Ryals, Renee, Clément, Nathalie, Cleaver, Brian, McDoom, Issam, Boye, Shannon E., Peden, Marc C., Sherwood, Mark B., Abernathy, Corinne R., Alkuraya, Fowzan S., Boye, Sanford L., Hauswirth, William W.
Vydáno 2013