Rescue of Pyruvate Kinase Deficiency in Mice by Gene Therapy Using the Human Isoenzyme

מאת Meza, Nestor W, Alonso-Ferrero, Maria E, Navarro, Susana, Quintana-Bustamante, Oscar, Valeri, Antonio, Garcia-Gomez, Maria, Bueren, Juan A, Bautista, Jose M, Segovia, Jose C
יצא לאור 2009

Enhancement of mouse hematopoietic stem/progenitor cell function via transient gene delivery using integration-deficient lentiviral vectors

מאת Alonso-Ferrero, Maria E., van Til, Niek P., Bartolovic, Kerol, Mata, Márcia F., Wagemaker, Gerard, Moulding, Dale, Williams, David A., Kinnon, Christine, Waddington, Simon N., Milsom, Michael D., Howe, Steven J.
הוצא לאור ב Exp Hematol (2018)

Systemic gene delivery following intravenous administration of AAV9 to fetal and neonatal mice and late-gestation nonhuman primates

מאת Mattar, Citra N., Wong, Andrew M. S., Hoefer, Klemens, Alonso-Ferrero, Maria E., Buckley, Suzanne M. K., Howe, Steven J., Cooper, Jonathan D., Waddington, Simon N., Chan, Jerry K. Y., Rahim, Ahad A.
הוצא לאור ב FASEB J (2015)

Perforin Gene Transfer Into Hematopoietic Stem Cells Improves Immune Dysregulation in Murine Models of Perforin Deficiency

מאת Carmo, Marlene, Risma, Kimberly A, Arumugam, Paritha, Tiwari, Swati, Hontz, Adrianne E, Montiel-Equihua, Claudia A, Alonso-Ferrero, Maria E, Blundell, Michael P, Schambach, Axel, Baum, Christopher, Malik, Punam, Thrasher, Adrian J, Jordan, Michael B, Gaspar, H Bobby
הוצא לאור ב Mol Ther (2015)

The β-Globin Locus Control Region in Combination With the EF1α Short Promoter Allows Enhanced Lentiviral Vector-mediated Erythroid Gene Expression With Conserved Multilineage Activ...

מאת Montiel-Equihua, Claudia A, Zhang, Lin, Knight, Sean, Saadeh, Heba, Scholz, Simone, Carmo, Marlene, Alonso-Ferrero, Maria E, Blundell, Michael P, Monkeviciute, Aiste, Schulz, Reiner, Collins, Mary, Takeuchi, Yasuhiro, Schmidt, Manfred, Fairbanks, Lynette, Antoniou, Michael, Thrasher, Adrian J, Gaspar, H Bobby
יצא לאור 2012