Development of gene therapy: potential in severe combined immunodeficiency due to adenosine deaminase deficiency

द्वारा Montiel-Equihua, Claudia A, Thrasher, Adrian J, Gaspar, H Bobby
प्रकाशित 2009

Perforin Gene Transfer Into Hematopoietic Stem Cells Improves Immune Dysregulation in Murine Models of Perforin Deficiency

द्वारा Carmo, Marlene, Risma, Kimberly A, Arumugam, Paritha, Tiwari, Swati, Hontz, Adrianne E, Montiel-Equihua, Claudia A, Alonso-Ferrero, Maria E, Blundell, Michael P, Schambach, Axel, Baum, Christopher, Malik, Punam, Thrasher, Adrian J, Jordan, Michael B, Gaspar, H Bobby
में प्रकाशित Mol Ther (2015)

The β-Globin Locus Control Region in Combination With the EF1α Short Promoter Allows Enhanced Lentiviral Vector-mediated Erythroid Gene Expression With Conserved Multilineage Activ...

द्वारा Montiel-Equihua, Claudia A, Zhang, Lin, Knight, Sean, Saadeh, Heba, Scholz, Simone, Carmo, Marlene, Alonso-Ferrero, Maria E, Blundell, Michael P, Monkeviciute, Aiste, Schulz, Reiner, Collins, Mary, Takeuchi, Yasuhiro, Schmidt, Manfred, Fairbanks, Lynette, Antoniou, Michael, Thrasher, Adrian J, Gaspar, H Bobby
प्रकाशित 2012