Rescue of Pyruvate Kinase Deficiency in Mice by Gene Therapy Using the Human Isoenzyme

Por Meza, Nestor W, Alonso-Ferrero, Maria E, Navarro, Susana, Quintana-Bustamante, Oscar, Valeri, Antonio, Garcia-Gomez, Maria, Bueren, Juan A, Bautista, Jose M, Segovia, Jose C
Publicado em 2009

Enhancement of mouse hematopoietic stem/progenitor cell function via transient gene delivery using integration-deficient lentiviral vectors

Por Alonso-Ferrero, Maria E., van Til, Niek P., Bartolovic, Kerol, Mata, Márcia F., Wagemaker, Gerard, Moulding, Dale, Williams, David A., Kinnon, Christine, Waddington, Simon N., Milsom, Michael D., Howe, Steven J.
Publicado no Exp Hematol (2018)

Systemic gene delivery following intravenous administration of AAV9 to fetal and neonatal mice and late-gestation nonhuman primates

Por Mattar, Citra N., Wong, Andrew M. S., Hoefer, Klemens, Alonso-Ferrero, Maria E., Buckley, Suzanne M. K., Howe, Steven J., Cooper, Jonathan D., Waddington, Simon N., Chan, Jerry K. Y., Rahim, Ahad A.
Publicado no FASEB J (2015)

Perforin Gene Transfer Into Hematopoietic Stem Cells Improves Immune Dysregulation in Murine Models of Perforin Deficiency

Por Carmo, Marlene, Risma, Kimberly A, Arumugam, Paritha, Tiwari, Swati, Hontz, Adrianne E, Montiel-Equihua, Claudia A, Alonso-Ferrero, Maria E, Blundell, Michael P, Schambach, Axel, Baum, Christopher, Malik, Punam, Thrasher, Adrian J, Jordan, Michael B, Gaspar, H Bobby
Publicado no Mol Ther (2015)

The β-Globin Locus Control Region in Combination With the EF1α Short Promoter Allows Enhanced Lentiviral Vector-mediated Erythroid Gene Expression With Conserved Multilineage Activ...

Por Montiel-Equihua, Claudia A, Zhang, Lin, Knight, Sean, Saadeh, Heba, Scholz, Simone, Carmo, Marlene, Alonso-Ferrero, Maria E, Blundell, Michael P, Monkeviciute, Aiste, Schulz, Reiner, Collins, Mary, Takeuchi, Yasuhiro, Schmidt, Manfred, Fairbanks, Lynette, Antoniou, Michael, Thrasher, Adrian J, Gaspar, H Bobby
Publicado em 2012