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Rational Design of Small Molecules to Enhance Genome Editing Efficiency by Selectively Targeting Distinct Functional States of CRISPR-Cas12a

CRISPR-Cas12a, a type-V CRISPR-Cas endonuclease, is an effective genome editing platform. To improve the gene editing efficiency of Cas12a, we rationally designed small molecule enhancers through a combined computational approach. First, we used extensive molecular dynamics (MD) simulations to explo...

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Detalhes bibliográficos
Publicado no:Bioconjug Chem
Main Authors: Li, Wenqing, Chan, Chun, Zeng, Chunxi, Turk, Rolf, Behlke, Mark A., Cheng, Xiaolin, Dong, Yizhou
Formato: Artigo
Idioma:Inglês
Publicado em: 2020
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC8192075/
https://ncbi.nlm.nih.gov/pubmed/32119776
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1021/acs.bioconjchem.0c00062
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