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Kinetics of HTT lowering in brain of YAC 128 mice following single and repetitive intranasal dosing of siRNA packaged in chitosan-based nanoparticle

This report describes the kinetics of Huntington’s Disease (HD) gene (HTT) lowering in brains of YAC 128 mice. Lowering (or “knock-down”) of HTT mRNA expression was achieved by intranasal administration of specially designed siRNA loaded into chitosan nanoparticles. Kinetic patterns of HTT lowering...

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Bibliografske podrobnosti
izdano v:J Drug Deliv Sci Technol
Main Authors: Sava, V., Fihurka, O., Khvorova, A., Sanchez-Ramos, J.
Format: Artigo
Jezik:Inglês
Izdano: 2021
Teme:
Online dostop:https://ncbi.nlm.nih.gov/pmc/articles/PMC8128136/
https://ncbi.nlm.nih.gov/pubmed/34012478
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.jddst.2021.102517
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