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Point estimation for adaptive trial designs II: Practical considerations and guidance

In adaptive clinical trials, the conventional end‐of‐trial point estimate of a treatment effect is prone to bias, that is, a systematic tendency to deviate from its true value. As stated in recent FDA guidance on adaptive designs, it is desirable to report estimates of treatment effects that reduce...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:Stat Med
Egile Nagusiak: Robertson, David S., Choodari‐Oskooei, Babak, Dimairo, Munya, Flight, Laura, Pallmann, Philip, Jaki, Thomas
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: John Wiley & Sons, Inc. 2023
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC7614609/
https://ncbi.nlm.nih.gov/pubmed/37021359
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/sim.9734
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