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Nonsequential Splicing Events Alter Antisense-Mediated Exon Skipping Outcome in COL7A1

The COL7A1 gene encodes homotrimer fibrils essential for anchoring dermal and epidermal layers, and pathogenic mutations in COL7A1 can cause recessive or dominant dystrophic epidermolysis bullosa. As a monogenic disease gene, COL7A1 constitutes a potential target for antisense oligomer-mediated exon...

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Detalles Bibliográficos
Publicado en:Int J Mol Sci
Main Authors: Ham, Kristin A., Aung-Htut, May Thandar, Fletcher, Sue, Wilton, Steve D.
Formato: Artigo
Idioma:Inglês
Publicado: MDPI 2020
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Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC7590164/
https://ncbi.nlm.nih.gov/pubmed/33081018
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ijms21207705
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