Lataa...

Genome Editing-Mediated Utrophin Upregulation in Duchenne Muscular Dystrophy Stem Cells

Utrophin upregulation is considered a promising therapeutic strategy for Duchenne muscular dystrophy (DMD). A number of microRNAs (miRNAs) post-transcriptionally regulate utrophin expression by binding their cognate sites in the 3′ UTR. Previously we have shown that miRNA: UTRN repression can be all...

Täydet tiedot

Tallennettuna:
Bibliografiset tiedot
Julkaisussa:Mol Ther Nucleic Acids
Päätekijät: Sengupta, Kasturi, Mishra, Manoj K., Loro, Emanuele, Spencer, Melissa J., Pyle, April D., Khurana, Tejvir S.
Aineistotyyppi: Artigo
Kieli:Inglês
Julkaistu: American Society of Gene & Cell Therapy 2020
Aiheet:
Linkit:https://ncbi.nlm.nih.gov/pmc/articles/PMC7554652/
https://ncbi.nlm.nih.gov/pubmed/33230452
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.omtn.2020.08.031
Tagit: Lisää tagi
Ei tageja, Lisää ensimmäinen tagi!