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Current landscape of treatments for Wolfram syndrome
Wolfram syndrome is a rare genetic spectrum disorder characterized by insulin-dependent diabetes mellitus, optic nerve atrophy and progressive neurodegeneration and ranges from mild to severe clinical symptoms. There is currently no treatment to delay, halt, or reverse the progression of Wolfram syn...
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| Yayımlandı: | Trends Pharmacol Sci |
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| Asıl Yazarlar: | , |
| Materyal Türü: | Artigo |
| Dil: | Inglês |
| Baskı/Yayın Bilgisi: |
2019
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| Konular: | |
| Online Erişim: | https://ncbi.nlm.nih.gov/pmc/articles/PMC7547529/ https://ncbi.nlm.nih.gov/pubmed/31420094 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.tips.2019.07.011 |
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