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Disruption of a key ligand-H-bond network drives dissociative properties in vamorolone for Duchenne muscular dystrophy treatment

Duchenne muscular dystrophy is a genetic disorder that shows chronic and progressive damage to skeletal and cardiac muscle leading to premature death. Antiinflammatory corticosteroids targeting the glucocorticoid receptor (GR) are the current standard of care but drive adverse side effects such as d...

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Pubblicato in:Proc Natl Acad Sci U S A
Autori principali: Liu, Xu, Wang, Yashuo, Gutierrez, Jennifer S., Damsker, Jesse M., Nagaraju, Kanneboyina, Hoffman, Eric P., Ortlund, Eric A.
Natura: Artigo
Lingua:Inglês
Pubblicazione: National Academy of Sciences 2020
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC7533876/
https://ncbi.nlm.nih.gov/pubmed/32917814
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1073/pnas.2006890117
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