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Population Pharmacokinetics of Vamorolone (VBP15) in Healthy Men and Boys with Duchenne Muscular Dystrophy

Duchenne muscular dystrophy (DMD) is an inherited neuromuscular disorder occurring in boys and caused by mutations in the dystrophin gene. Vamorolone is a first-generation delta-9,11 compound that has favorable efficacy and side effect profiles relative to classical glucocorticoids. The pharmacokine...

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Detalles Bibliográficos
Publicado en:J Clin Pharmacol
Main Authors: Mavroudis, Panteleimon D., van den Anker, John, Conklin, Laurie S., Damsker, Jesse M., Hoffman, Eric P., Nagaraju, Kanneboyina, Clemens, Paula R., Jusko, William J.
Formato: Artigo
Idioma:Inglês
Publicado: 2019
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Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC6548694/
https://ncbi.nlm.nih.gov/pubmed/30742306
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/jcph.1388
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