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From Ivacaftor to Triple Combination: A Systematic Review of Efficacy and Safety of CFTR Modulators in People with Cystic Fibrosis

Over the last years CFTR (cystic fibrosis transmembrane conductance regulator) modulators have shown the ability to improve relevant clinical outcomes in patients with cystic fibrosis (CF). This review aims at a systematic research of the current evidence on efficacy and tolerability of CFTR modulat...

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Podrobná bibliografie
Vydáno v:Int J Mol Sci
Hlavní autoři: Gramegna, Andrea, Contarini, Martina, Aliberti, Stefano, Casciaro, Rosaria, Blasi, Francesco, Castellani, Carlo
Médium: Artigo
Jazyk:Inglês
Vydáno: MDPI 2020
Témata:
On-line přístup:https://ncbi.nlm.nih.gov/pmc/articles/PMC7461566/
https://ncbi.nlm.nih.gov/pubmed/32824306
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ijms21165882
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