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From Ivacaftor to Triple Combination: A Systematic Review of Efficacy and Safety of CFTR Modulators in People with Cystic Fibrosis

Over the last years CFTR (cystic fibrosis transmembrane conductance regulator) modulators have shown the ability to improve relevant clinical outcomes in patients with cystic fibrosis (CF). This review aims at a systematic research of the current evidence on efficacy and tolerability of CFTR modulat...

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Dettagli Bibliografici
Pubblicato in:Int J Mol Sci
Autori principali: Gramegna, Andrea, Contarini, Martina, Aliberti, Stefano, Casciaro, Rosaria, Blasi, Francesco, Castellani, Carlo
Natura: Artigo
Lingua:Inglês
Pubblicazione: MDPI 2020
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC7461566/
https://ncbi.nlm.nih.gov/pubmed/32824306
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ijms21165882
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