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Cystic fibrosis drug ivacaftor stimulates CFTR channels at picomolar concentrations

The devastating inherited disease cystic fibrosis (CF) is caused by mutations of the Cystic Fibrosis Transmembrane Conductance Regulator (CFTR) anion channel. The recent approval of the CFTR potentiator drug ivacaftor (Vx-770) for the treatment of CF patients has marked the advent of causative CF th...

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Publicat a:eLife
Autors principals: Csanády, László, Töröcsik, Beáta
Format: Artigo
Idioma:Inglês
Publicat: eLife Sciences Publications, Ltd 2019
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Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6594753/
https://ncbi.nlm.nih.gov/pubmed/31205003
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.7554/eLife.46450
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