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Cytosine base editor generates substantial off-target single-nucleotide variants in mouse embryos

Genome editing holds promise for correcting pathogenic mutations. However, it is difficult to determine off-target effects of editing due to single-nucleotide polymorphism in individuals. Here we developed a method named GOTI (genome-wide off-target analysis by two-cell embryo injection) to detect o...

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Библиографические подробности
Опубликовано в: :Science
Главные авторы: Zuo, Erwei, Sun, Yidi, Wei, Wu, Yuan, Tanglong, Ying, Wenqin, Sun, Hao, Yuan, Liyun, Steinmetz, Lars M., Li, Yixue, Yang, Hui
Формат: Artigo
Язык:Inglês
Опубликовано: 2019
Предметы:
Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC7301308/
https://ncbi.nlm.nih.gov/pubmed/30819928
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1126/science.aav9973
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