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Inhalation delivery technology for genome-editing of respiratory diseases

The clustered regulatory interspaced short palindromic repeats (CRISPR)/CRISPR-associated protein 9 (CRISPR/Cas9) system has significant therapeutic potentials for lung congenital diseases such as cystic fibrosis, as well as other pulmonary disorders like lung cancer and obstructive diseases. Local...

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Dettagli Bibliografici
Pubblicato in:Adv Drug Deliv Rev
Autori principali: Chow, Michael Y.T., Chang, Rachel Yoon Kyung, Chan, Hak-Kim
Natura: Artigo
Lingua:Inglês
Pubblicazione: Elsevier B.V. 2021
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC7274121/
https://ncbi.nlm.nih.gov/pubmed/32512029
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.addr.2020.06.001
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