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Target selectivity in mRNA silencing

Despite the excitement and promise of RNA interference in treating neurodegenerative disease, disease gene mRNA might resist mRNA silencing. Conventional siRNA design does not uniformly distinguish a mutant from a wild-type allele. CAG expansions in trinucleotide repeat diseases are unselective targ...

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Dades bibliogràfiques
Publicat a:Gene Ther
Autor principal: Aronin, N
Format: Artigo
Idioma:Inglês
Publicat: Nature Publishing Group UK 2006
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC7091803/
https://ncbi.nlm.nih.gov/pubmed/16520821
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/sj.gt.3302726
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