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Pathogenic Mechanisms and Therapy Development for C9orf72 Amyotrophic Lateral Sclerosis/Frontotemporal Dementia

In 2011, a hexanucleotide repeat expansion in the first intron of the C9orf72 gene was identified as the most common genetic cause of amyotrophic lateral sclerosis (ALS) and frontotemporal dementia (FTD). The proposed disease mechanisms include loss of C9orf72 function and gain of toxicity from the...

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Bibliographic Details
Published in:Neurotherapeutics
Main Authors: Jiang, Jie, Ravits, John
Format: Artigo
Language:Inglês
Published: Springer International Publishing 2019
Subjects:
Online Access:https://ncbi.nlm.nih.gov/pmc/articles/PMC6985338/
https://ncbi.nlm.nih.gov/pubmed/31667754
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s13311-019-00797-2
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