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Familial Hemophagocytic Lymphohistiocytosis: A Rare Mutation of STXBP2 in Exon 19

Familial hemophagocytic lymphohistiocytosis (FHLH) is a fulminant rapidly progressive disorder characterized by uncontrolled immune system activation. Over the last decade, STXBP2 mutations have been reported as causative. We report a baby with typical clinical features and supportive laboratory fin...

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Publicado en:J Pediatr Genet
Autores principales: Pournami, Femitha, Upadhyay, Swati, Nandakumar, Anand, Prabhakar, Jyothi, Jain, Naveen
Formato: Artigo
Lenguaje:Inglês
Publicado: Georg Thieme Verlag KG 2020
Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC6976306/
https://ncbi.nlm.nih.gov/pubmed/31976148
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1055/s-0039-1694778
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