Nalaganje...

An AAV Dual Vector Strategy Ameliorates the Stargardt Phenotype in Adult Abca4(−/−) Mice

The recent approval in the United States of the first adeno-associated viral (AAV) vector for the treatment of an inherited retinal degeneration validates this approach for the treatment of many other diseases. A major limiting factor continues to be the size restriction of the AAV transgene at unde...

Popoln opis

Shranjeno v:
Bibliografske podrobnosti
izdano v:Hum Gene Ther
Main Authors: McClements, Michelle E., Barnard, Alun R., Singh, Mandeep S., Charbel Issa, Peter, Jiang, Zhichun, Radu, Roxana A., MacLaren, Robert E.
Format: Artigo
Jezik:Inglês
Izdano: Mary Ann Liebert, Inc., publishers 2019
Teme:
Online dostop:https://ncbi.nlm.nih.gov/pmc/articles/PMC6909730/
https://ncbi.nlm.nih.gov/pubmed/30381971
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/hum.2018.156
Oznake: Označite
Brez oznak, prvi označite!