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A fragmented adeno-associated viral dual vector strategy for treatment of diseases caused by mutations in large genes leads to expression of hybrid transcripts

OBJECTIVE: Dual vector AAV systems are being utilised to enable gene therapy for disorders in which the disease gene is too large to fit into a single capsid. Fragmented adeno-associated viral (fAAV) vectors containing single inverted terminal repeat truncated transgenes have been considered as one...

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Detalhes bibliográficos
Publicado no:J Genet Syndr Gene Ther
Main Authors: McClements, Michelle E., Charbel Issa, Peter, Blouin, Véronique, MacLaren, Robert E.
Formato: Artigo
Idioma:Inglês
Publicado em: 2016
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5321474/
https://ncbi.nlm.nih.gov/pubmed/28239514
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.4172/2157-7412.1000311
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