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AAV-mediated delivery of CRISPR/Cas systems for genome engineering in mammalian cells

The CRISPR/Cas9 system has emerged as a highly versatile platform for inducing targeted genome modifications into mammalian cells and model organisms. However, fully capitalizing on the therapeutic potential for this system requires its safe and efficient delivery into relevant cell types. Adeno-ass...

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Detalles Bibliográficos
Publicado en:Cold Spring Harb Protoc
Autores principales: Gaj, Thomas, Schaffer, David V.
Formato: Artigo
Lenguaje:Inglês
Publicado: 2016
Materias:
Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC6850213/
https://ncbi.nlm.nih.gov/pubmed/27803249
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1101/pdb.prot086868
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