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Advances in gene therapy for cystic fibrosis lung disease
Cystic fibrosis (CF) is a multiorgan recessive genetic disease caused by mutations in the cystic fibrosis transmembrane conductance regulator (CFTR) gene. Gene therapy efforts have focused on treating the lung, since it manifests the most significant life-threatening disease. Over two decades have p...
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| Pubblicato in: | Hum Mol Genet |
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| Autori principali: | , , |
| Natura: | Artigo |
| Lingua: | Inglês |
| Pubblicazione: |
Oxford University Press
2019
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| Soggetti: | |
| Accesso online: | https://ncbi.nlm.nih.gov/pmc/articles/PMC6796993/ https://ncbi.nlm.nih.gov/pubmed/31332440 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/hmg/ddz139 |
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