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Motoneuron Transplantation Rescues the Phenotype of SMARD1 (Spinal Muscular Atrophy with Respiratory Distress Type 1)

Spinal muscular atrophy with respiratory distress type 1 (SMARD1) is a fatal form of infantile motoneuron disease. There is currently no effective treatment, although motor neuron replacement is a possible therapeutic strategy. We transplanted purified motor neurons into the spinal cord of nmd mice,...

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Vydáno v:J Neurosci
Hlavní autoři: Corti, Stefania, Nizzardo, Monica, Nardini, Martina, Donadoni, Chiara, Salani, Sabrina, Del Bo, Roberto, Papadimitriou, Dimitra, Locatelli, Federica, Mezzina, Nicoletta, Gianni, Francesca, Bresolin, Nereo, Comi, Giacomo P.
Médium: Artigo
Jazyk:Inglês
Vydáno: Society for Neuroscience 2009
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On-line přístup:https://ncbi.nlm.nih.gov/pmc/articles/PMC6666655/
https://ncbi.nlm.nih.gov/pubmed/19776263
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1523/JNEUROSCI.2734-09.2009
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