Genetic Correction of Human Induced Pluripotent Stem Cells from Patients with Spinal Muscular Atrophy

Spinal muscular atrophy (SMA) is among the most common genetic neurological diseases that cause infant mortality. Induced pluripotent stem cells (iPSCs) generated from skin fibroblasts from SMA patients and genetically corrected have been proposed to be useful for autologous cell therapy. We generat...

Full description

Saved in:
Bibliographic Details
Published in:Sci Transl Med
Main Authors: Corti, Stefania, Nizzardo, Monica, Simone, Chiara, Falcone, Marianna, Nardini, Martina, Ronchi, Dario, Donadoni, Chiara, Salani, Sabrina, Riboldi, Giulietta, Magri, Francesca, Menozzi, Giorgia, Bonaglia, Clara, Rizzo, Federica, Bresolin, Nereo, Comi, Giacomo P.
Format: Artigo
Language:Inglês
Published: 2012
Subjects:
Article
Online Access:https://ncbi.nlm.nih.gov/pmc/articles/PMC4722730/
https://ncbi.nlm.nih.gov/pubmed/23253609
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1126/scitranslmed.3004108
Tags: Add Tag
No Tags, Be the first to tag this record!

Similar Items