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Adenovirus-mediated ABCC6 Gene Therapy for Heritable Ectopic Mineralization Disorders

Loss-of-function mutations in the ABCC6 gene cause pseudoxanthoma elasticum (PXE) and type 2 generalized arterial calcification of infancy (GACI), heritable ectopic mineralization disorders without effective treatment. ABCC6 encodes the putative efflux transporter ABCC6 which is predominantly expres...

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Detalles Bibliográficos
Publicado en:J Invest Dermatol
Autores principales: Huang, Jianhe, Snook, Adam E., Uitto, Jouni, Li, Qiaoli
Formato: Artigo
Lenguaje:Inglês
Publicado: 2019
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC6535136/
https://ncbi.nlm.nih.gov/pubmed/30639429
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.jid.2018.12.017
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