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Cell specific delivery of modified mRNA expressing therapeutic proteins to leukocytes

Therapeutic alteration of gene expression in vivo can be achieved by delivering nucleic acids (e.g., mRNA, siRNA) using nanoparticles. Recent progress in modified messenger RNA (mmRNA) synthesis facilitated the development of lipid nanoparticles (LNPs) loaded with mmRNA as a promising tool for in vi...

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Detalles Bibliográficos
Publicado en:Nat Commun
Main Authors: Veiga, Nuphar, Goldsmith, Meir, Granot, Yasmin, Rosenblum, Daniel, Dammes, Niels, Kedmi, Ranit, Ramishetti, Srinivas, Peer, Dan
Formato: Artigo
Idioma:Inglês
Publicado: Nature Publishing Group UK 2018
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Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC6206083/
https://ncbi.nlm.nih.gov/pubmed/30374059
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/s41467-018-06936-1
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