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Impaired mitochondrial dynamics underlie axonal defects in hereditary spastic paraplegias

Mechanisms by which long corticospinal axons degenerate in hereditary spastic paraplegia (HSP) are largely unknown. Here, we have generated induced pluripotent stem cells (iPSCs) from patients with two autosomal recessive forms of HSP, SPG15 and SPG48, which are caused by mutations in the ZFYVE26 an...

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Dettagli Bibliografici
Pubblicato in:Hum Mol Genet
Autori principali: Denton, Kyle, Mou, Yongchao, Xu, Chong-Chong, Shah, Dhruvi, Chang, Jaerak, Blackstone, Craig, Li, Xue-Jun
Natura: Artigo
Lingua:Inglês
Pubblicazione: Oxford University Press 2018
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC6031053/
https://ncbi.nlm.nih.gov/pubmed/29726929
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/hmg/ddy156
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