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Therapy development in Huntington disease: From current strategies to emerging opportunities

Huntington disease (HD) is a progressive autosomal dominant neurodegenerative disorder in which patients typically present with uncontrolled involuntary movements and subsequent cognitive decline. In 1993, a CAG trinucleotide repeat expansion in the coding region of the huntingtin (HTT) gene was ide...

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Dettagli Bibliografici
Pubblicato in:Am J Med Genet A
Autori principali: Dickey, Audrey S., La Spada, Albert R.
Natura: Artigo
Lingua:Inglês
Pubblicazione: 2017
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC5975251/
https://ncbi.nlm.nih.gov/pubmed/29218782
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/ajmg.a.38494
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