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Precise Excision of the CAG Tract from the Huntingtin Gene by Cas9 Nickases

Huntington's disease (HD) is a progressive autosomal dominant neurodegenerative disorder caused by the expansion of CAG repeats in the first exon of the huntingtin gene (HTT). The accumulation of polyglutamine-rich huntingtin proteins affects various cellular functions and causes selective dege...

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Dettagli Bibliografici
Pubblicato in:Front Neurosci
Autori principali: Dabrowska, Magdalena, Juzwa, Wojciech, Krzyzosiak, Wlodzimierz J., Olejniczak, Marta
Natura: Artigo
Lingua:Inglês
Pubblicazione: Frontiers Media S.A. 2018
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC5834764/
https://ncbi.nlm.nih.gov/pubmed/29535594
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3389/fnins.2018.00075
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