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Application of polyploid adeno-associated virus vectors for transduction enhancement and neutralizing antibody evasion

Adeno-associated virus (AAV) vectors have been used successfully in clinical trials for patients with hemophilia or blindness, but pre-existing neutralizing antibodies (Nab) are common in the general population and exclude many patients from clinical trials. Exploration of effective strategies to en...

Täydet tiedot

Tallennettuna:
Bibliografiset tiedot
Julkaisussa:J Control Release
Päätekijät: Chai, Zheng, Sun, Junjiang, Rigsbee, Kelly Michelle, Wang, Mei, Samulski, R. Jude, Li, Chengwen
Aineistotyyppi: Artigo
Kieli:Inglês
Julkaistu: 2017
Aiheet:
Linkit:https://ncbi.nlm.nih.gov/pmc/articles/PMC5819605/
https://ncbi.nlm.nih.gov/pubmed/28789965
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.jconrel.2017.08.005
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