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Altered Cellular Homeostasis in Murine MPS I Fibroblasts: Evidence of Cell-Specific Physiopathology

Mucopolysaccharidosis type I (MPS I), a rare autosomal recessive disease, is caused by a deficiency of the lysosomal enzyme alfa-l-iduronidase. Impaired enzyme activity promotes glycosaminoglycans accumulation in several tissues and organs, leading to complex multisystemic complications. Several stu...

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Detalhes bibliográficos
Publicado no:JIMD Rep
Main Authors: Viana, Gustavo Monteiro, do Nascimento, Cinthia Castro, Paredes-Gamero, Edgar Julian, D’Almeida, Vânia
Formato: Artigo
Idioma:Inglês
Publicado em: Springer Berlin Heidelberg 2017
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5680293/
https://ncbi.nlm.nih.gov/pubmed/28220405
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/8904_2017_5
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