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Neonatal umbilical cord blood transplantation halts skeletal disease progression in the murine model of MPS-I

Umbilical cord blood (UCB) is a promising source of stem cells to use in early haematopoietic stem cell transplantation (HSCT) approaches for several genetic diseases that can be diagnosed at birth. Mucopolysaccharidosis type I (MPS-I) is a progressive multi-system disorder caused by deficiency of l...

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Detaylı Bibliyografya
Yayımlandı:Sci Rep
Asıl Yazarlar: Azario, Isabella, Pievani, Alice, Del Priore, Federica, Antolini, Laura, Santi, Ludovica, Corsi, Alessandro, Cardinale, Lucia, Sawamoto, Kazuki, Kubaski, Francyne, Gentner, Bernhard, Bernardo, Maria Ester, Valsecchi, Maria Grazia, Riminucci, Mara, Tomatsu, Shunji, Aiuti, Alessandro, Biondi, Andrea, Serafini, Marta
Materyal Türü: Artigo
Dil:Inglês
Baskı/Yayın Bilgisi: Nature Publishing Group UK 2017
Konular:
Online Erişim:https://ncbi.nlm.nih.gov/pmc/articles/PMC5573317/
https://ncbi.nlm.nih.gov/pubmed/28842642
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/s41598-017-09958-9
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