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Neonatal umbilical cord blood transplantation halts skeletal disease progression in the murine model of MPS-I

Umbilical cord blood (UCB) is a promising source of stem cells to use in early haematopoietic stem cell transplantation (HSCT) approaches for several genetic diseases that can be diagnosed at birth. Mucopolysaccharidosis type I (MPS-I) is a progressive multi-system disorder caused by deficiency of l...

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Dades bibliogràfiques
Publicat a:Sci Rep
Autors principals: Azario, Isabella, Pievani, Alice, Del Priore, Federica, Antolini, Laura, Santi, Ludovica, Corsi, Alessandro, Cardinale, Lucia, Sawamoto, Kazuki, Kubaski, Francyne, Gentner, Bernhard, Bernardo, Maria Ester, Valsecchi, Maria Grazia, Riminucci, Mara, Tomatsu, Shunji, Aiuti, Alessandro, Biondi, Andrea, Serafini, Marta
Format: Artigo
Idioma:Inglês
Publicat: Nature Publishing Group UK 2017
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC5573317/
https://ncbi.nlm.nih.gov/pubmed/28842642
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/s41598-017-09958-9
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