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Neonatal umbilical cord blood transplantation halts skeletal disease progression in the murine model of MPS-I

Umbilical cord blood (UCB) is a promising source of stem cells to use in early haematopoietic stem cell transplantation (HSCT) approaches for several genetic diseases that can be diagnosed at birth. Mucopolysaccharidosis type I (MPS-I) is a progressive multi-system disorder caused by deficiency of l...

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Detalles Bibliográficos
Publicado en:Sci Rep
Main Authors: Azario, Isabella, Pievani, Alice, Del Priore, Federica, Antolini, Laura, Santi, Ludovica, Corsi, Alessandro, Cardinale, Lucia, Sawamoto, Kazuki, Kubaski, Francyne, Gentner, Bernhard, Bernardo, Maria Ester, Valsecchi, Maria Grazia, Riminucci, Mara, Tomatsu, Shunji, Aiuti, Alessandro, Biondi, Andrea, Serafini, Marta
Formato: Artigo
Idioma:Inglês
Publicado: Nature Publishing Group UK 2017
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Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC5573317/
https://ncbi.nlm.nih.gov/pubmed/28842642
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/s41598-017-09958-9
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